LMI070

LMI070, also called as NVS-SM1, is a selective, high plasma exposure and orally active modulator of SMN2 splicing which demonstrates robust activity across disease-relevant induced pluripotent stem cell (iPSc)-derived neurons.
in vivo: oral administration
Supplier BOC Sciences
Product # 1562338-42-4
Pricing Inquire
Cas 1562338-42-4
Molecular Weight 393.48
Molecular Formula C22H27N5O2
Canonical SMILES CC1(CC(CC(N1)(C)C)OC2=NNC(=C3C=CC(=CC3=O)C4=CNN=C4)C=C2)C
Feedback